European Hematology Association - Genetic Modification of Autologous Hematopoietic Stem Cells: A Potential Treatment for Mucopolysaccharidosis Type I Hurler

The results of this study will be presented by Professor Maria Ester Bernardo in the Presidential Symposium. The results of this study will be presented by ProfessorMaria Ester Bernardoin the Presidential Symposium. Presenter:   ProfessorMaria Ester Bernardo Affiliation:   Ospedale San Raffaele,Milan, Italy Abstract:  #S102 HEMATOPOIETIC STEM CELL-GENE THERAPY FOR MUCOPOLYSACCHARIDOSIS TYPE I, HURLER: EVIDENCE OF EXTENSIVE METABOLIC CORRECTION AND EARLY CLINICAL...

The results of this study will be presented by Professor Maria Ester Bernardo in the Presidential Symposium.

Presenter:  Professor Maria Ester Bernardo

Affiliation:  Ospedale San Raffaele, Milan, Italy

Abstract:  #S102  HEMATOPOIETIC STEM CELL-GENE THERAPY FOR MUCOPOLYSACCHARIDOSIS TYPE I, HURLER: EVIDENCE OF EXTENSIVE METABOLIC CORRECTION AND EARLY CLINICAL RESPONSE

About the EHA Annual Congress: Every June, EHA organizes its Annual Congress in a major European city. This year, due to the persisting COVID19 pandemic, EHA organizes a virtual Congress for the second time. The Congress is aimed at health professionals working in or interested in the field of hematology. The scientific program topics range from stem cell physiology and development to leukemia; lymphoma; diagnosis and treatment; red blood cells; white blood cells and platelet disorders; hemophilia and myeloma; thrombosis and bleeding disorders; as well as transfusion and stem cell transplantation.

Website: www.ehaweb.org

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